• Long-term follow-up of renal function in patients treated with migalastat for Fabry disease 

      Bichet, Daniel G.; Torra, Roser; Wallace, Eric; Hughes, Derralynn A.; Giugliani, Roberto; Skuban, Nina; Krusinska, Eva; Feldt-Rasmussen, Ulla; Schiffmann, Raphael; Nicholls, Kathy (2021) [Artigo de periódico]
      The effect of migalastat on long-term renal outcomes in enzyme replacement therapy (ERT)–naive and ERTexperienced patients with Fabry disease is not well defined. An integrated posthoc analysis of the phase 3 clinical ...