Navegação Ciências Biológicas por Assunto "JR-141"

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    • Iduronate-2-sulfatase fused with anti-hTfR antibody, pabinafusp alfa, for MPS-II : a phase 2 trial in Brazil 

      Giugliani, Roberto; Martins, Ana Maria (Medicina); So, Sairei; Yamamoto, Tatsuyoshi; Yamaoka, Mariko; Ikeda, Toshiaki; Tanizawa, Kazunori; Sonoda, Hiroyuki; Schmidt, Mathias; Sato, Yuji (2021) [Artigo de periódico]
      In Hunter syndrome (mucopolysaccharidosis II [MPS-II]),systemic accumulation of glycosaminoglycans (GAGs) dueto a deficiency of iduronate-2-sulfatase (IDS), caused by mu-tations in theIDSgene, leads to multiple somatic ...