Navegação Ciências da Saúde por Autor "Mulberg, Andrew E."

Resultados 1-1 de 1

    • Migalastat improves diarrhea in patients with Fabry disease : clinical-biomarker correlations from the phase 3 FACETS trial 

      Schiffmann, Raphael; Bichet, Daniel G.; Jovanovic, Ana; Hughes, Derralynn A.; Giugliani, Roberto; Feldt-Rasmussen, Ulla; Shankar, S. P.; Barisoni, Laura; Colvin, Robert B.; Jennette, J. Charles; Holdbrook, Fred; Mulberg, Andrew E.; Castelli, Jeffrey P.; Skuban, Nina; Barth, Jay; Nicholls, Kathleen M. (2018) [Artigo de periódico]
      Background: Fabry disease is frequently characterized by gastrointestinal symptoms, including diarrhea. Migalastat is an orally-administered small molecule approved to treat the symptoms of Fabry disease in patients with ...