Browsing Health Sciences by Subject "Long-term effectiveness"
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Long-term outcomes with agalsidase alfa enzyme replacement therapy : analysis using deconstructed composite events
(2017) [Journal article]This is a retrospective analysis of Fabry Outcome Survey data from children/adults (n =677) receiving agalsidase alfa enzyme replacement therapy for a median of 3 years, examining cerebrovascular, cardiac, and renal morbidity ...